@misc
{TN_libero_mab2,
author = {
Cohen-Haguenauer, Odile
Aiuti, Alessandro
AND
Ali, Robin R.
AND
Alici, Evren
AND
Almqvist, Per
AND
Annunziata, Patrizia
AND
Anton, Martina
AND
Artus, Alexandre
AND
Athanasopoulos, Takis
AND
Aubourg, Patrick
AND
Auregan, Gwennaelle
AND
Auricchio, Alberto
AND
Bandeira, Vanessa
AND
Bartholomae, Cynthia C.
AND
Baum, Christopher
AND
Bayart, Émilie
AND
Bednarski, Christien
AND
Bellier, Bertrand
AND
Biasco, Luca
AND
Bigey, Pascal
AND
Blouin, Véronique
AND
Bode, Juergen
AND
Bonvento, Gilles
AND
Bosch, Fatima
AND
Bougnères, Pierre
AND
Brigida, Immacolata
AND
Broll, Sandra
AND
Buchholz, Christian J.
AND
Bureau, Michel-Francis
AND
Bárcia, Rita N.
AND
Callejas, David
AND
Carina Silva, Ana
AND
Carrondo, Manuel J.T
AND
Cartier, Nathalie
AND
Cathomen, Toni
AND
Cavazzana-Calvo, Marina
AND
Chuah, Marinee K.L
AND
Cichutek, Klaus
AND
Cohen-Haguenauer, Odile
AND
Colin, Angélique
AND
Cordova, Gonzalo
AND
Coroadinha, Ana Sofia
AND
Cosset, François-Loïc
AND
Cotugno, Gabriella
AND
Cruz, Helder J.S
AND
Cruz, Pedro E.
AND
Darmon, Christophe
AND
Davidoff, Andrew M.
AND
Dickson, George
AND
Dittmar, Kurt E.J
AND
Draghia-Akli, Ruxandra
AND
Dufour, Noëlle
AND
Duros, Caroline
AND
Déglon, Nicole
AND
Dürner, Lydia
AND
Eriksdotter-Jönhagen, Maria
AND
Escartin, Carole
AND
Escriou, Virginie
AND
Eyjolfsdottir, Helga
AND
Faideau, Mathilde
AND
Fischer, Alain
AND
Foster, Helen
AND
Foster, Keith
AND
Gahrton, Gösta
AND
Galla, Melanie
AND
Galy, Anne
AND
Gama-Norton, Leonor
AND
Garritsen, Henk S.P
AND
Georgiadis, Anastasios
AND
Giacca, Mauro
AND
Gilljam, Mari
AND
Gänsbacher, Bernd
AND
Hacein-Bey-Abina, Salima
AND
Hantraye, Philippe
AND
Haskins, Mark
AND
Hassig, Raymonde
AND
Hauser, Hansjörg
AND
Heinz, Niels
AND
Händel, Eva-Maria
AND
Ivics, Zoltán
AND
Izsvák, Zsuzsanna
AND
Jacobs, Andreas H.
AND
Jarmin, Susan
AND
Jimenez, Veronica
AND
Kalle, Christof von
AND
Kang, Jagjeet
AND
Kent, Alastair
AND
Khalaileh, Abed
AND
Kichler, Antoine
AND
King, Nancy M.P
AND
Klatzmann, David
AND
Kochanek, Stefan
AND
Kolodkin-Gal, Dror
AND
Koo, Taeyoung
AND
Kunicher, Nikolai
AND
Lachmann, Kristina
AND
Laufs, Stephanie
AND
Lemaire, Stéphanie
AND
Lemoine, François
AND
Lind, Göran
AND
Lindenmaier, Werner
AND
Linderoth, Bengt
AND
Lock, Martin
AND
Lucas, Tanja
AND
Luzzatto, Lucio
AND
Macke, Lars
AND
Maetzig, Tobias
AND
Maldiney, Thomas
AND
Malerba, Alberto
AND
Mann, Christopher
AND
Marie, Corinne
AND
Marques Alves, Paula
AND
Merten, Otto-Wilhelm
AND
Meyring, Wilhelm
AND
Mignet, Nathalie
AND
Mingozzi, Federico
AND
Mitrophanous, Kyriacos
AND
Modlich, Ute
AND
Monfared, Parisa
AND
Montini, Eugenio
AND
Moullier, Philippe
AND
Naldini, Luigi
AND
Nathwani, Amit C.
AND
Nienhuis, Arthur W.
AND
Palfi, Stéphane
AND
Panet, Amos
AND
Peixoto, Cristina
AND
Pohl, Susanne
AND
Popplewell, Linda
AND
Pâques, Frédéric
AND
Raj, Deepak
AND
Ralph, R. Scott
AND
Reiss, Ulrike
AND
Richard, Cyrille
AND
Rischmüller, Anja
AND
Rodrigues, Ana F.
AND
Rosenzwajg, Michelle
AND
Santos, Jorge M.
AND
Schambach, Axel
AND
Schaser, Thomas
AND
Scherman, Daniel
AND
Schleef, Martin
AND
Schmeer, Marco
AND
Schmidt, Manfred
AND
Schweizer, Matthias
AND
Schäfers, Sonja
AND
Seiger, Åke
AND
Simão, Daniel
AND
Six, Adrien
AND
Smith, Alexander J
AND
Smith, Alexander J.
AND
Smith, Julianne
AND
Snyder, Richard O.
AND
Sofia Coroadinha, Ana
AND
Sousa, Marcos F.Q
AND
Suerth, Julia D.
AND
Sundström, Erik
AND
Tayeb, Shay
AND
Thomas, Michael
AND
Thomas-Vaslin, Véronique
AND
Tuddenham, Edward G.D
AND
VandenDriessche, Thierry
AND
Verhoeyen, Els
AND
Verma, Inder M.
AND
Viel, Thomas
AND
Waerzeggers, Yannic
AND
Wahlberg, Lars
AND
Winkeler, Alexandra
AND
Wirth, Dagmar
AND
Ylä-Herttuala, Seppo
AND
Zacchigna, Serena
AND
Zamir, Gidi
},
title = {
The CliniBook
Clinical gene transfer state of the art
},
publisher = {EDP Sciences},
publisher = {},
isbn = {9782842542375},
keywords = {
Genetic transformation
,
MEDICAL / Laboratory Medicine
},
year = {[2012]},
year = {, ©2012},
abstract = {Frontmatter},
abstract = {CliniGene Partners and Boards},
abstract = {ACKNOWLEDGMENTS},
abstract = {List of authors},
abstract = {Contents},
abstract = {INTRODUCTION},
abstract = {In-1 Foreword},
abstract = {In-2 Main achievements and prospects downstream of the CliniGene-NoE},
abstract = {PART I: TECHNOLOGIES AND PRE-CLINICAL STUDIES},
abstract = {TECHNOLOGIES - Highlights on AAV mediated gene transfer},
abstract = {A1-1 Highlights on AAV mediated gene transfer: introduction},
abstract = {A1-2 Preclinical studies of AAV gene therapy for inherited retinal dystrophies},
abstract = {A1-3 AAV-mediated gene therapy for MPS VI},
abstract = {A1-4 Microdystrophin and myostatin gene therapy for Duchenne muscular dystrophy using adeno-associated virus vectors},
abstract = {A1-5 AAV gene therapy for cardiovascular disorders},
abstract = {A1-6 AAV gene therapy for diabetes mellitus},
abstract = {A1-7 Approaches to large scale production of AAV-vectors},
abstract = {A1-8 Reference materials for the characterization of adeno-associated viral vectors},
abstract = {TECHNOLOGIES - Retrovirus mediated gene transfer state-of-the-art},
abstract = {A2-1 Highlights on retrovirus mediated gene transfer},
abstract = {A2-2 Retroviral vector development: reducing genotoxicity of integrated DNA and creating virus-like particles for transient cell modification},
abstract = {A2-3 Replication-competent y-retroviral vectors for tumor therapy},
abstract = {A2-4 Modular retroviral producer cell lines},
abstract = {TECHNOLOGIES - Highlights on lentivirus mediated gene transfer},
abstract = {A3-1 Introduction},
abstract = {A3-2 MicroRNAs detargeting technology in the context of CNS applications},
abstract = {A3-3 Development of SIVsmmPBj vectors for gene transfer into myeloid cells},
abstract = {A3-4 Insulated retrovirus vectors using novel synthetic genetic insulator elements to circumvent enhancer-mediated genotoxicity},
abstract = {A3-5 Facing the challenges of downstream processing of lentiviral vectors},
abstract = {A3-6 Restrictions and requirements for stable lentiviral vector production in HEK293 cells},
abstract = {A3-7 Novel lentiviral vector pseudotypes for stable gene transfer into resting hematopoietic cells},
abstract = {TECHNOLOGIES - Highlights on gene-modified cell therapy},
abstract = {A4-1 Cell therapy Introduction},
abstract = {A4-2 Ex-vivo expansion of human mesenchymal stem cells},
abstract = {A4-3 Closed bag cultivation systems for the production of gene modified dendritic cells and MSC for clinical use},
abstract = {A4-4 Genetically modified NK cells for cancer treatment: facts and visions},
abstract = {A4-5 Regulatory T lymphocyte depletion for cancer immunotherapies},
abstract = {A4-6 Gene therapy of Fanconi’s anaemia aplastic syndrome},
abstract = {TECHNOLOGIES - Adenovirus mediated gene transfer: current developments},
abstract = {A5-1 Overview on adenovirus vectors},
abstract = {A5-2 Tumour barriers influencing adenovirus vector delivery and therapeutic efficacy},
abstract = {A5-3 Tumor imaging with adenoviral vectors},
abstract = {A5-4 Treatment of brain tumors with adenoviruses: preclinical development},
abstract = {A5-5 Production and purification of Ad vectors: current status and future needs for adenovirus vector production},
abstract = {TECHNOLOGIES - Non-viral based gene transfer: a new era},
abstract = {A6-1 Non viral plasmid delivery and imaging of transgene expression A6-1 Non viral plasmid delivery and imaging of transgene expression},
abstract = {A6-2 Overview of novel plasmid vectors and preclinical applications},
abstract = {A6-3 Filling a gap: S/MAR-based replicating minicircles},
abstract = {A6-4 Manufacturing and QC of plasmid based vectors},
abstract = {A6-5 Sleeping Beauty transposon based gene therapy},
abstract = {A6-6 Development of minicircle vectors},
abstract = {A6-7 Exon skipping therapy for DMD using antisense oligomer technology},
abstract = {TECHNOLOGIES - Highlights on emerging technologies, iPS induction and genetic stability},
abstract = {A7-1 Induction of pluripotency from adult somatic cells: a review},
abstract = {A7-2 Genetic modification of adult stem cells and induced pluripotent stem cells with emerging transposon technologies},
abstract = {A7-3 Targeted genome engineering approaches based on rare-cutting endonucleases: a tentative summary},
abstract = {A7-4 Targeted genome modifications with designer nucleases},
abstract = {B1-1 Preclinical assessment tools: imaging gene transfer to the brain},
abstract = {B1-2 Persistent luminescence nanoparticles for in vivo imaging: characteristics and targeting},
abstract = {B1-3 Ex-vivo evaluation of gene-transfer vectors: efficacy, tropism and safety},
abstract = {B2-1 Assessing and taming unwanted immune responses induced by AAV gene transfer: current status, ongoing questions and future prospects},
abstract = {B2-2 Predicting immune responses to viral vectors and transgenes in gene therapy and vaccination: the coming of systems biology},
abstract = {B2-3 Biosafety analysis in preclinical and clinical studies},
abstract = {PART II Clinical trials and regulatory issues},
abstract = {CLINICAL TRIALS},
abstract = {C1-1 A clinical trial of AAV-mediated gene therapy for Leber congenital amaurosis 2},
abstract = {C1-2 Gene therapy for X-linked adrenoleukodystrophy based on lentiviral correction of hematopoietic stem cells},
abstract = {C1-3 Immune reconstitution after gene therapy for adenosine deaminase severe combined immunodeficiency (ADA-SCID)},
abstract = {C1-4 Gene therapy in Alzheimer disease patients},
abstract = {C1-5 Cardiovascular gene therapy trials},
abstract = {C1-6 AAV-mediated gene therapy for haemophilia B},
abstract = {C1-7 ProSavin®: a lentiviral vector approach for the treatment of Parkinson’s disease},
abstract = {ETHICAL AND REGULATORY ISSUES},
abstract = {C2-1 Ethics in translation from research to therapy},
abstract = {C2-2 Centralised regulation of gene therapy in Europe},
abstract = {C2-3 The necessity for data sharing towards advancement of clinical translation Building up sample IMPD* and substantiating master files},
abstract = {INTEGRATION AND DISSEMINATION},
abstract = {C3-1 European Union support to gene transfer and gene therapy},
abstract = {C3-2 Database of clinical trials},
abstract = {C3-3 CliniGene and ESGCT shared vision for gene therapy in Europe: past, present and future prospects},
abstract = {AUTHOR INDEX},
address = {
Les Ulis
,
},
url = {
http://slubdd.de/katalog?TN_libero_mab2
}
}