@misc
{TN_libero_mab2,
author = {
Kishnani, Priya S.
AND
Diaz-Manera, Jordi
AND
Toscano, Antonio
AND
Clemens, Paula R.
AND
Ladha, Shafeeq
AND
Berger, Kenneth I.
AND
Kushlaf, Hani
AND
Straub, Volker
AND
Carvalho, Gerson
AND
Mozaffar, Tahseen
AND
Roberts, Mark
AND
Attarian, Shahram
AND
Chien, Yin-Hsiu
AND
Choi, Young-Chul
AND
Day, John W.
AND
Erdem-Ozdamar, Sevim
AND
Illarioshkin, Sergey
AND
Goker-Alpan, Ozlem
AND
Kostera-Pruszczyk, Anna
AND
van der Ploeg, Ans T.
AND
An Haack, Kristina
AND
Huynh-Ba, Olivier
AND
Tammireddy, Swathi
AND
Thibault, Nathan
AND
Zhou, Tianyue
AND
Dimachkie, Mazen M.
AND
Schoser, Benedikt
AND
Behin, Anthony
AND
Boentert, Matthias
AND
Carvalho, Gerson
AND
Chahin, Nizar
AND
Charrow, Joel
AND
Deegan, Patrick
AND
Durmus Tekce, Hacer
AND
Duval, Fanny
AND
Genge, Angela
AND
Gutmann, Ludwig
AND
Henderson, Robert D.
AND
Hennermann, Julia B.
AND
Hiwot, Tarekegn
AND
Hughes, Derralynn
AND
Karaa, Amel
AND
Karam, Chafic
AND
Kautzky-Willer, Alexandra
AND
Komaki, Hirofumi
AND
Laforet, Pascal
AND
Longo, Nicola
AND
Malinova, Vera
AND
Maré, Ricardo
AND
Maxit, Clarisa
AND
Mengel, Eugen
AND
Moggio, Maurizio Gualtiero
AND
Molnár, Mária Judit
AND
Mongini, Tiziana Enrica
AND
Nadaj-Pakleza, Aleksandra
AND
Nascimento Osorio, Andres
AND
Noury, Jean-Baptiste
AND
Oliveira, Acary Souza Bulle
AND
Parman, Yesim
AND
Pena, Loren
AND
Remiche, Gauthier
AND
Sciacco, Monica
AND
Shieh, Perry B. Shieh
AND
Smith, Cheryl
AND
Stulnig, Thomas
AND
Taithe, Frederic
AND
Tard, Céline
AND
Tarnopolsky, Mark
AND
Vorgerd, Matthias
AND
Whitley, Chester
AND
Young, Peter
AND
Alonso-Pérez, Jorge
AND
Altemus, Patricia
AND
Aubé-Nathier, Anne-Catherine
AND
Avelar, Jennifer B.
AND
Bailey, Carrie
AND
Bekircan-Kurt, Can Ebru
AND
Billy, Jenny
AND
Boschi, Silvia
AND
Brown, Kathryn E.
AND
Carrera Garcia, Laura
AND
Chase, Lauren
AND
Cirne, Hamilton
AND
Danjoux, Loïc
AND
Davion, Jean-Baptiste
AND
DeArmey, Stephanie
AND
Fedotova, Ekaterina
AND
Gandolfo, Eve
AND
Grosz, Zoltan
AND
Guellec, Dewi
AND
Guettsches, Anne-Katrin
AND
Guglieri, Michela
AND
Hatcher, Erin
AND
Helms, Sina
AND
Hufgard-Leitner, Miriam
AND
Klyushnikov, Sergey A.
AND
Langton, Jacqui
AND
Linková, Lenka
AND
Mavroudakis, Nicolas
AND
Mazurová, Stella
AND
Mori, Madoka
AND
Müller-Miny, Louisa
AND
Musumeci, Olimpia
AND
Nance, Christopher S.
AND
Natera-de Benito, Daniel
AND
Neel, Robert
AND
Niizawa, Gabriela A.
AND
Noll, Lauren
AND
Ortega, Erik
AND
Pasnoor, Mamatha
AND
Pautot, Vivien
AND
Potulska-Chromik, Anna
AND
Pugliese, Alessia
AND
Questienne, Claire
AND
Ramos Lopes, Margarida
AND
Reyes-Leiva, David
AND
Riedl, Michaela
AND
Rugiero, Marcelo Francisco
AND
Salort-Campana, Emmanuelle
AND
Sgobbi Souza, Paulo Victor
AND
Sole, Guilhem
AND
Solera, Luca
AND
Souto Lopes, Suzara
AND
Specht, Sabine
AND
Statland, Jeffrey
AND
Swenson, Andrea
AND
Tan, Chong Yew
AND
Tizon, Sónia
AND
van der Beek, N.A.M.E.
AND
van Kooten, Harmke A.
AND
Wencel, Marie
AND
Wenninger, Stephan
AND
Zagnoli, Fabien
},
title = {
Efficacy and Safety of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease After 97 Weeks : A Phase 3 Randomized Clinical Trial
A Phase 3 Randomized Clinical Trial
},
publisher = {American Medical Association (AMA)},
isbn = {2168-6149},
keywords = {
Neurology (clinical)
},
year = {2023},
url = {
http://slubdd.de/katalog?TN_libero_mab2
}
}