@misc {TN_libero_mab2,
author = { Kishnani, Priya S. AND Diaz-Manera, Jordi AND Toscano, Antonio AND Clemens, Paula R. AND Ladha, Shafeeq AND Berger, Kenneth I. AND Kushlaf, Hani AND Straub, Volker AND Carvalho, Gerson AND Mozaffar, Tahseen AND Roberts, Mark AND Attarian, Shahram AND Chien, Yin-Hsiu AND Choi, Young-Chul AND Day, John W. AND Erdem-Ozdamar, Sevim AND Illarioshkin, Sergey AND Goker-Alpan, Ozlem AND Kostera-Pruszczyk, Anna AND van der Ploeg, Ans T. AND An Haack, Kristina AND Huynh-Ba, Olivier AND Tammireddy, Swathi AND Thibault, Nathan AND Zhou, Tianyue AND Dimachkie, Mazen M. AND Schoser, Benedikt AND Behin, Anthony AND Boentert, Matthias AND Carvalho, Gerson AND Chahin, Nizar AND Charrow, Joel AND Deegan, Patrick AND Durmus Tekce, Hacer AND Duval, Fanny AND Genge, Angela AND Gutmann, Ludwig AND Henderson, Robert D. AND Hennermann, Julia B. AND Hiwot, Tarekegn AND Hughes, Derralynn AND Karaa, Amel AND Karam, Chafic AND Kautzky-Willer, Alexandra AND Komaki, Hirofumi AND Laforet, Pascal AND Longo, Nicola AND Malinova, Vera AND Maré, Ricardo AND Maxit, Clarisa AND Mengel, Eugen AND Moggio, Maurizio Gualtiero AND Molnár, Mária Judit AND Mongini, Tiziana Enrica AND Nadaj-Pakleza, Aleksandra AND Nascimento Osorio, Andres AND Noury, Jean-Baptiste AND Oliveira, Acary Souza Bulle AND Parman, Yesim AND Pena, Loren AND Remiche, Gauthier AND Sciacco, Monica AND Shieh, Perry B. Shieh AND Smith, Cheryl AND Stulnig, Thomas AND Taithe, Frederic AND Tard, Céline AND Tarnopolsky, Mark AND Vorgerd, Matthias AND Whitley, Chester AND Young, Peter AND Alonso-Pérez, Jorge AND Altemus, Patricia AND Aubé-Nathier, Anne-Catherine AND Avelar, Jennifer B. AND Bailey, Carrie AND Bekircan-Kurt, Can Ebru AND Billy, Jenny AND Boschi, Silvia AND Brown, Kathryn E. AND Carrera Garcia, Laura AND Chase, Lauren AND Cirne, Hamilton AND Danjoux, Loïc AND Davion, Jean-Baptiste AND DeArmey, Stephanie AND Fedotova, Ekaterina AND Gandolfo, Eve AND Grosz, Zoltan AND Guellec, Dewi AND Guettsches, Anne-Katrin AND Guglieri, Michela AND Hatcher, Erin AND Helms, Sina AND Hufgard-Leitner, Miriam AND Klyushnikov, Sergey A. AND Langton, Jacqui AND Linková, Lenka AND Mavroudakis, Nicolas AND Mazurová, Stella AND Mori, Madoka AND Müller-Miny, Louisa AND Musumeci, Olimpia AND Nance, Christopher S. AND Natera-de Benito, Daniel AND Neel, Robert AND Niizawa, Gabriela A. AND Noll, Lauren AND Ortega, Erik AND Pasnoor, Mamatha AND Pautot, Vivien AND Potulska-Chromik, Anna AND Pugliese, Alessia AND Questienne, Claire AND Ramos Lopes, Margarida AND Reyes-Leiva, David AND Riedl, Michaela AND Rugiero, Marcelo Francisco AND Salort-Campana, Emmanuelle AND Sgobbi Souza, Paulo Victor AND Sole, Guilhem AND Solera, Luca AND Souto Lopes, Suzara AND Specht, Sabine AND Statland, Jeffrey AND Swenson, Andrea AND Tan, Chong Yew AND Tizon, Sónia AND van der Beek, N.A.M.E. AND van Kooten, Harmke A. AND Wencel, Marie AND Wenninger, Stephan AND Zagnoli, Fabien },
title = { Efficacy and Safety of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease After 97 Weeks : A Phase 3 Randomized Clinical Trial A Phase 3 Randomized Clinical Trial },
publisher = {American Medical Association (AMA)},
isbn = {2168-6149},
keywords = { Neurology (clinical) },
year = {2023},
url = { http://slubdd.de/katalog?TN_libero_mab2 }
}
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