%0 Generic
%T Efficacy and Safety of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease After 97 Weeks : A Phase 3 Randomized Clinical Trial A Phase 3 Randomized Clinical Trial
%A Kishnani, Priya S.
%A Diaz-Manera, Jordi
%A Toscano, Antonio
%A Clemens, Paula R.
%A Ladha, Shafeeq
%A Berger, Kenneth I.
%A Kushlaf, Hani
%A Straub, Volker
%A Carvalho, Gerson
%A Mozaffar, Tahseen
%A Roberts, Mark
%A Attarian, Shahram
%A Chien, Yin-Hsiu
%A Choi, Young-Chul
%A Day, John W.
%A Erdem-Ozdamar, Sevim
%A Illarioshkin, Sergey
%A Goker-Alpan, Ozlem
%A Kostera-Pruszczyk, Anna
%A van der Ploeg, Ans T.
%A An Haack, Kristina
%A Huynh-Ba, Olivier
%A Tammireddy, Swathi
%A Thibault, Nathan
%A Zhou, Tianyue
%A Dimachkie, Mazen M.
%A Schoser, Benedikt
%A Behin, Anthony
%A Boentert, Matthias
%A Carvalho, Gerson
%A Chahin, Nizar
%A Charrow, Joel
%A Deegan, Patrick
%A Durmus Tekce, Hacer
%A Duval, Fanny
%A Genge, Angela
%A Gutmann, Ludwig
%A Henderson, Robert D.
%A Hennermann, Julia B.
%A Hiwot, Tarekegn
%A Hughes, Derralynn
%A Karaa, Amel
%A Karam, Chafic
%A Kautzky-Willer, Alexandra
%A Komaki, Hirofumi
%A Laforet, Pascal
%A Longo, Nicola
%A Malinova, Vera
%A Maré, Ricardo
%A Maxit, Clarisa
%A Mengel, Eugen
%A Moggio, Maurizio Gualtiero
%A Molnár, Mária Judit
%A Mongini, Tiziana Enrica
%A Nadaj-Pakleza, Aleksandra
%A Nascimento Osorio, Andres
%A Noury, Jean-Baptiste
%A Oliveira, Acary Souza Bulle
%A Parman, Yesim
%A Pena, Loren
%A Remiche, Gauthier
%A Sciacco, Monica
%A Shieh, Perry B. Shieh
%A Smith, Cheryl
%A Stulnig, Thomas
%A Taithe, Frederic
%A Tard, Céline
%A Tarnopolsky, Mark
%A Vorgerd, Matthias
%A Whitley, Chester
%A Young, Peter
%A Alonso-Pérez, Jorge
%A Altemus, Patricia
%A Aubé-Nathier, Anne-Catherine
%A Avelar, Jennifer B.
%A Bailey, Carrie
%A Bekircan-Kurt, Can Ebru
%A Billy, Jenny
%A Boschi, Silvia
%A Brown, Kathryn E.
%A Carrera Garcia, Laura
%A Chase, Lauren
%A Cirne, Hamilton
%A Danjoux, Loïc
%A Davion, Jean-Baptiste
%A DeArmey, Stephanie
%A Fedotova, Ekaterina
%A Gandolfo, Eve
%A Grosz, Zoltan
%A Guellec, Dewi
%A Guettsches, Anne-Katrin
%A Guglieri, Michela
%A Hatcher, Erin
%A Helms, Sina
%A Hufgard-Leitner, Miriam
%A Klyushnikov, Sergey A.
%A Langton, Jacqui
%A Linková, Lenka
%A Mavroudakis, Nicolas
%A Mazurová, Stella
%A Mori, Madoka
%A Müller-Miny, Louisa
%A Musumeci, Olimpia
%A Nance, Christopher S.
%A Natera-de Benito, Daniel
%A Neel, Robert
%A Niizawa, Gabriela A.
%A Noll, Lauren
%A Ortega, Erik
%A Pasnoor, Mamatha
%A Pautot, Vivien
%A Potulska-Chromik, Anna
%A Pugliese, Alessia
%A Questienne, Claire
%A Ramos Lopes, Margarida
%A Reyes-Leiva, David
%A Riedl, Michaela
%A Rugiero, Marcelo Francisco
%A Salort-Campana, Emmanuelle
%A Sgobbi Souza, Paulo Victor
%A Sole, Guilhem
%A Solera, Luca
%A Souto Lopes, Suzara
%A Specht, Sabine
%A Statland, Jeffrey
%A Swenson, Andrea
%A Tan, Chong Yew
%A Tizon, Sónia
%A van der Beek, N.A.M.E.
%A van Kooten, Harmke A.
%A Wencel, Marie
%A Wenninger, Stephan
%A Zagnoli, Fabien
%I American Medical Association (AMA)
%@ 2168-6149
%D 2023
%C American Medical Association (AMA)
%U http://slubdd.de/katalog?TN_libero_mab2
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