• Media type: E-Article
  • Title: Iduronate-2-sulfatase transport vehicle rescues behavioral and skeletal phenotypes in a mouse model of Hunter syndrome
  • Contributor: Arguello, Annie; Meisner, René; Thomsen, Elliot R.; Nguyen, Hoang N.; Ravi, Ritesh; Simms, Jeffrey; Lo, Iris; Speckart, Jessica; Holtzman, Julia; Gill, Thomas M.; Chan, Darren; Cheng, Yuhsiang; Chiu, Chi-Lu; Dugas, Jason C.; Fang, Meng; Lopez, Isabel A.; Solanoy, Hilda; Tsogtbaatar, Buyankhishig; Zhu, Yuda; Bhalla, Akhil; Henne, Kirk R.; Henry, Anastasia G.; Delucchi, Anthony; Costanzo, Simona; [...]
  • imprint: American Society for Clinical Investigation, 2021
  • Published in: JCI Insight
  • Language: English
  • DOI: 10.1172/jci.insight.145445
  • ISSN: 2379-3708
  • Origination:
  • Footnote:
  • Access State: Open Access