• Media type: E-Article
  • Title: Molecular evaluation and vector integration analysis of HCC complicating AAV gene therapy for hemophilia B
  • Contributor: Schmidt, Manfred; Foster, Graham R.; Coppens, Michiel; Thomsen, Hauke; Dolmetsch, Ricardo; Heijink, Liesbeth; Monahan, Paul E.; Pipe, Steven W.
  • imprint: American Society of Hematology, 2023
  • Published in: Blood Advances
  • Language: English
  • DOI: 10.1182/bloodadvances.2023009876
  • ISSN: 2473-9537; 2473-9529
  • Origination:
  • Footnote:
  • Access State: Open Access